Gene editing treats a mouse model of a neurodevelopmental disorder
Yang, K. et al. Nature https://doi.org/10.1038/s41586-026-10113-6 (2026).Article
Google Scholar
Alendar, A. & Berns, A. Gene Dev. 35, 1403–1430 (2021).Article
PubMed
Google Scholar
Gillentine, M. A., Wang, T. & Eichler, E. E. Biomedicines 10, 2865 (2022).Article
PubMed
Google Scholar
Drivas, T. G. et al. Eur. J. Hum. Genet. 28, 1422–1431 (2020).Article
PubMed
Google Scholar
Almeida, M. C. et al. Neuron 112, 1778–1794 (2024).Article
PubMed
Google Scholar
Coe, B. P. et al. Nature Genet. 51, 106–116 (2019).Article
PubMed
Google Scholar
Musunuru, K. et al. N. Engl. J. Med. 392, 2235–2243 (2025).Article
PubMed
Google Scholar
Wang, C. et al. Nature Mater. 24, 1653–1663 (2025).Article
PubMed
Google Scholar